Research and Treatment

Research & Treatment

After years of excitement about a possible “one-and-done” treatment, gene therapy uptake has been slower than expected. Here’s why.
Similar to biologic medications, this type of therapy is safe and effective and could expand your access to treatment.
The wearable wellness device works without medications or hormones and complements other bleeding disorder treatments.
This rebalancing agent can help people with hemophilia A or B — with or without inhibitors — to better control...
You only get one chance. Cutting-edge gene therapies that show the most promise for a permanent solution to hemophilia rely...
Roshni Kulkarni, M.D., recalls a time when a patient was attacked by a wild turkey and wanted advice about whether...
Remote work, remote learning, remote meetups with friends — Americans have gotten much more comfortable conducting critical (and noncritical) tasks...
Since 1966, leading immunologists, clinicians and researchers in gene therapy have been convening every one to three years to discuss...
After several decades of research, gene therapy for hemophilia is moving closer to becoming a reality. One of the most...
On two rainy days in May 2018, more than 200 researchers, clinicians, pharmaceutical industry representatives, government officials, and patient advocates...
For Sol Schulman, MD, PhD, a principal investigator in the Division of Hemostasis and Thrombosis at Beth Israel Deaconess Medical...
Brandon Downey, 32, a nurse in Chicago with severe hemophilia A, has switched treatments several times over the last decade...
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